Tot who 'would survive just seven months' is turning three and learning to walk from gene xx Watch Video

⏲ Duration: 4:4
👁 View: 185K times
✓ Published: 15-Mar-2024

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A little boy born with a severe muscle condition who doctors said would survive just seven months is turning three - and now learning to walk.<br/><br/>Rupert Mosey, two, developed spinal muscular atrophy (SMA) soon after birth - a condition causing muscle degeneration.<br/><br/>Doctors warned his parents, Charlie Mosey, 36, and her husband, George, 39, that the tot wouldn't live past seven months old.<br/><br/>But at three months old he had a miracle gene therapy drug Zolgensma - which dramatically reduced his muscle wastage.<br/><br/>Five months later he was enrolled on a clinical trial for a SMA treatment in Milan, Italy.<br/><br/>Doctors even made a special allowance for him to continue accessing the drug in the UK after the trial ended - due to his progress.<br/><br/>He was the first child with SMA to have the treatment, Spinraza, after having had Zolgensma, outside of a clinical trial and on the basis he's progressing well.<br/><br/>Charlie and George spend hours every day doing physical therapy with Rupert to help build his muscle strength - and it's paying off.<br/><br/>Incredibly, the tot has defied the odds to turn three this month and is even now learning to walk unaided.<br/><br/>Charlie, VP of customer success for a tech company, from St Albans, Hertfordshire, said: \